Researchers at National Taiwan University have developed a liver-directed IL-10 gene therapy that strengthens cancer-fighting ...

Three 2026 Breakthrough Prize winners reflect on developing Luxturna, a gene therapy that treats blindness caused by rare ...

A first-of-its-kind gene therapy that can restore hearing in children born deaf has just cleared its final hurdle—and, in a ...

The agency's decision is based on results from a clinical trial in which the treatment improved hearing in 80 percent of the ...

Sarepta stock toppled Thursday as investors digested the better-than-feared sales of its beleaguered gene therapy, Elevidys.

Kelly Anne is a deputy editor at Forbes Advisor overseeing the development of various initiatives, including newsletters, ...

Saffie Sandford was born with Leber's Congenital Amaurosis and "missed out on a lot" due to difficulties seeing in any ...

The FDA has approved Otarmeni, the first-ever gene therapy for genetic hearing loss caused by the OTOF gene, for both ...

LONDON -- A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on her own, two years after the treatment. Opal Sandy made history in 2023 when ...

Groundbreaking AAV-based gene therapy offers potential treatment for patients with OTOF gene-associated severe-to-profound and profound hearing lossWhite Oak, Md., April 24, 2026 (GLOBE NEWSWIRE) -- ...

Stuart Orkin and Swee Lay Thein shared a Breakthrough Prize in Life Sciences for their research on genetic causes of sickle ...

Researchers use hIL-6 protein to restore walking in paralyzed mice by promoting neural circuit plasticity rather than fiber regrowth.