A research team led by scientists at Cincinnati Children’s Hospital has uncovered a new potential approach to preventing the muscle-wasting symptoms of muscular dystrophy (MD), a family of genetic ...
Researchers at the Experimental and Clinical Research Center (ECRC), a joint institution of the Max Delbrück Center and Charité—Universitätsmedizin Berlin, have developed a promising gene-editing ...
Scientists have developed a novel approach of genome editing to repair muscle stem (satellite) cells, offering new hope for ...
A cell therapy preserves muscle structure and function in laboratory mice with a type of disease similar to Duchenne muscular dystrophy, according to new research from the Smidt Heart Institute at ...
The scientists demonstrate that it is possible to specifically deliver the treatment to the muscle stem cells, avoiding accumulation in other organs. (Nanowerk News) In a collaboration between the ...
The muscular dystrophies are characterized by progressive weakness and wasting of striated muscle and are caused by inherited or de novo gene mutation of sarcolemma-associated proteins or nuclear ...
The MDA's 75th anniversary conference highlights advancements in gene therapy, precision medicine, and patient-centered care for muscular dystrophy. Discussions focus on equitable access to ...
Please provide your email address to receive an email when new articles are posted on . New therapies for muscular dystrophy must go beyond traditional corticosteroid administration. Treatments that ...
Left: Muscle fibers expressing dysferlin (purple) made from gene-edited muscle stem cells transplanted into a mouse that lacks dysferlin. Right: Muscle fibers from the recipient mouse that are ...
There is no cure for DMD, but treatments can slow the progression of the disease and help improve quality of life. Duchenne muscular dystrophy (DMD) is a chronic condition that causes a gradual loss ...
NEW YORK -- Stem-cell injections worked remarkably well at easing symptoms of muscular dystrophy in a group of golden retrievers, a result that experts call a significant step toward treating people. ...