Saffie Sandford was born with Leber's Congenital Amaurosis and "missed out on a lot" due to difficulties seeing in any ...

Gene therapy represents one of medicine’s most ambitious attempts to treat disease at its root cause by altering the genetic code itself. The approach works by recovering the functions of critical ...

You might like the sound of this news. In a landmark move, the Food and Drug Administration on Thursday approved the first gene therapy for a rare, inherited form of hearing loss. And while these ...

Spur Therapeutics today released new data from the GALILEO-1 and GALILEO-2 trials of avigbagene parvec (FLT201), its investigational gene therapy for Gaucher disease type 1 (GD1), which highlight ...

As cell and gene therapy leaders gathered in Maryland to discuss accelerating clinical trials in children, one “cutting edge” ...

The Greater Philadelphia Business Coalition on Health webinar series provided an in-depth framework for the advantages of including cell and gene therapy coverage in employer health plans, as well as ...

As other global companies race to find new gene therapies, Regeneron plans to make the new drug free for those in the US ...

Researchers at the Nora Eccles Harrison Cardiovascular Research and Training Institute, University of Utah, and the University of Utah School of Medicine, have demonstrated that a gene therapy can ...

Aradigm Health CEO Will Shrank discusses the shift in value-based care models for cell and gene therapies. While advances in ...

A new gene therapy tested in China has improved the hearing of 38 people who were born deaf due to mutations in a gene called OTOF.

Pharmaceutical Executive spoke with Aradigm Health CEO Will Shrank at the Asembia ASX26 Summit in Las Vegas. During the conversation, he explained the issues the payers face with cell & gene therapies ...

A gene found in salamanders could one day help humans regrow lost limbs, a breakthrough that sounds like science fiction but ...