FDA doesn’t approve leucovorin for autism. What can it be used for?

The FDA narrowed leucovorin's use to a rare disorder, a major shift after Trump and RFK Jr. promoted it for autism.

FDA clears repurposed GSK drug for ultra-rare brain disease instead of autism

Months after promising help for “hundreds of thousands of kids,” the FDA approved the decades-old medicine for a disease documented in less than 50 people.

FDA approves GSK’s Wellcovorin for cerebral folate deficiency

FDA worked with GSK to update Wellcovorin labelling for safe, effective use in adult and paediatric CFD-FOLR1 patients.
Scientific American

These cancers were beyond treatment—but might not be anymore

In the long and often dispiriting quest to cure cancer, the 1998 approval of the drug Herceptin was a tremendously hopeful moment. This drug for breast cancer was the first to use a tumor-specific ...