Spinraza (nusinersen) treatment helped school-age children with SMA be more independent in tasks involving their arms and ...

Needing help in the shower can be uncomfortable, says columnist Connie Chandler, but it's also allowed for vulnerability in ...

Columnist Kevin Schaefer explains that, in life with SMA, transitions and milestones look different from those of his ...

There is currently no cure for spinal muscular atrophy (SMA) yet, but there are a number of treatments that can delay the progression of symptoms, as well as several experimental treatments currently ...

Spinal muscular atrophy (SMA) is an inherited neurodegenerative disorder characterized by progressive muscle weakness. SMA patients do not produce enough of a protein called survival motor neuron (SMN ...

The SBMA therapy AJ201 showed good safety, hints of efficacy, and improved physical activity for this SMA type in a trial, ...