Injecting medicines into amniotic fluid may be a viable strategy for treating SMA before birth, according to a new study in ...

The SBMA therapy AJ201 showed good safety, hints of efficacy, and improved physical activity for this SMA type in a trial, ...

There is currently no cure for spinal muscular atrophy (SMA) yet, but there are a number of treatments that can delay the progression of symptoms, as well as several experimental treatments currently ...

Spinal muscular atrophy (SMA) is an inherited neurodegenerative disorder characterized by progressive muscle weakness. SMA patients do not produce enough of a protein called survival motor neuron (SMN ...