Sarepta Therapeutics said Friday that the deaths of two patients taking its marketed gene therapy Elevidys® (delandistrogene ...

Researchers say the new concept that lithium deficiency could be a cause of Alzheimer’s disease points to a different ...

Ocugen says it is on track to reshape the market for gene therapies against eye disorders over the next three years, by ...

Agg-CLNP synergized with abatacept to delay RA-related inflammation and with dexamethasone to prevent flare-ups following ...

HNF1A mutations are found to dysregulate RNA splicing in pancreatic cells, thereby contributing to the onset of diabetes.

Digitization has allowed Sanofi to optimize manufacturing and automate document preparation. And now, the firm predicts that ...

A new vaccine design pipeline could protect against emerging SARS-CoV-2 variants and pinpoint conserved T-cell epitopes across respiratory viruses.

“We propose that cysteinyl leukotrienes have dual functions in food allergy in mice by promoting mucosal mast cell expansion and by stimulating acute sensitization to oral anaphylaxis through ...

Researchers plan to collaborate on preclinical trials to apply polymersomes to real-world vaccine or drug delivery challenges.

The primary safety risks associated with gene therapy include immune reactions and off-target effects in unintended organs, ...

OpenCRISPR-1, an AI-generated custom gene editor capable of precision editing of the human genome. is just the beginning of ...

Researchers developed a method to dissect immune-regulatory programs via integrative time-series analysis and high-content CRISPR screening.